Rare diseases

In the USA, the most expensive medicine worth $2.8 million was approved. It will treat beta-thalassemia

Medicine against SMA is no longer the most expensive in the world. Their record was broken by gene therapy Zynteglo worth $2.8 million. August 17 FDA approved gene therapy from of the Bluebird Bio company, intended for the treatment of a rare disorder – beta-thalassemia, which causes a decrease in ... Read more